Department of Molecular Genetics & Microbiology

Barth syndrome stalks young patients, weakening heart and skeletal muscles, stunting growth and shortening their lives. University of Florida Health researchers and their colleagues have now discovered a promising solution:…

In the human nervous system, proteins, RNA and other cellular material need a free-flowing molecular highway. But when a “traffic jam” develops, the consequences are severe: One of several neurodegenerative…

A new gene therapy developed by University of Florida Health researchers stops vision loss and improves sight in dogs — a key step toward testing the treatment in people affected…

A new blood test could reveal the genetic roots of muscular dystrophy, amyotrophic lateral sclerosis and other disorders caused by the expansion of DNA repeats, potentially helping doctors diagnose their…